ALD-104 (CALD) Clinical study of the Lenti-D drug product (gene therapy) in boys with cerebral adrenoleukodystrophy - temporarily closed for inclusion
Long-term HIT (Stem cell transplantation) Clinical study investigating blood production in stem cell transplantation survivors - open for inclusion
PIKACHU (Stem cell transplantation) Clinical study of precision dosing of prednisolone as either prophylaxis or treatment of graft-versus-host disease after hematopoetic stem cell transplantation - open for inclusion
Tracing stem cells after transplantation Medical-scientific research on DNA mutations in stem cells to understand and improve blood formation after stem cell transplantation - temporarily closed for inclusion